0
  • Notifications
  • No notifications yet

  • View All Notifications
ChemDmart
Chemxpert Database
  • About
    • About
    • Leadership
    • Advisory Board
  • Products
    • ChemProtel - Product Intelligence
    • CompFolio - One Company Profile
    • CompGroupe - Group Company Profile
    • ChemScape - Data Landscape
    • ChemDmart - E-Market Place
    • DataIntel - Data Analytics/Trends
    • DataFeed - Data News/Feed
    • CompShow- Company Showcase
  • Sources
  • Subscription
  • User Guide
  • Contact
  • Book Demo Log In
  1. Home
  2. All News
  3. Novartis Receives Fda Breakthrough Therapy Designation For Rare Disease Med
News Feed
course image
  • 26 Nov 2021
  • Admin
  • News Article

Novartis Receives Fda Breakthrough Therapy Designation For Rare Disease Med

Swiss Pharma Company Novartis Has Received A Breakthrough Therapy Designation (Btd) For Its Experimental Medication Iptacopan For The Rare Blood Disorder Paroxysmal Nocturnal Hemoglobinuria (Pnh).The Therapy, Also Known As Lnp023, Was Also Awarded A Rare Paediatric Disease Designation At The Same Time For The Treatment Of C3 Glomerulopathy (C3G), A Group Of Ultra Rare Conditions That Can Cause End-Stage Renal Disease.Iptacopan Is An Oral Factor B Inhibitor And Is In Development Not Only For Pnh And C3G, But Also A Number Of Other Renal Conditions With Complement System Involvement.This Includes Iga Nephropathy (Igan), Atypical Hemolytic Uremic Syndrome (Ahus), And Membranous Nephropathy (Mn).The Btd Designation Was Based On The Positive Interim Results From Two Ongoing Phase 2 Studies, Within Which Iptacopan Demonstrated Benefits In Patients Who Remained Anaemic And Dependent On Transfusions, Despite Standard Of Care Anti-Complement Treatment, As Well As Monotherapy In Anti-C5 Naive Pnh Patients.In This Study, Iptacopan Significantly Reduced Proteinuria

Let’s apply Data-Driven Pricing to Your APIs

Sick and tired of always wondering if you are being asked to pay the right price for your APIs? This empowers you with the answers you need to make the right decisions in the Global API market.

Chemxpert Database is one of the biggest and most comprehensive directories of pharma and chemicals, manufacturers, suppliers and information. Provided with current information on prices, demand and transactions, it gives you instant feedback on whether you are buying what is right and at the right time.

Start using market intelligence today and allow yourself to be in control in the API market.

Check it out today and make more informed sourcing decisions! Learn More!

Categories

image
Product Related Updates
image
Certificates/Accreditation
image
Approval/Launch
image
Clinical Trial Update
image
Licensing/Partnering/Collaboration Deal
image
ODD/BTA/FTA Status
image
Merger/Acquisition
image
Warning/Recalls

Lifescience Intellipedia Pvt. Ltd.

C-89, Sector-65 Noida-U.P. 201301 (India)
Toll-Free: 18004190155
Phone: +91-120-6631301-361
Mobile: +91-9990237670
Email: info@lifescienceintellipedia.com
Email: sales@lifescienceintellipedia.com

USEFUL LINKS

  • Home
  • Privacy Policy
  • Terms & Conditions
  • Terms Of Use
  • Refund Policy
  • Blogs

OUR PRODUCTS

  • ChemProtel - Product Intelligence
  • CompFolio - One Company Profile
  • CompGroupe - Group Company Profile
  • ChemScape - Data Landscape
  • ChemDmart - E-Market Place
  • DataIntel - Data Analytics/Trends
  • DataFeed - Data News/Feed
  • CompShow- Company Showcase

LOCATION

© Copyright Lifescience Intellipedia Pvt. Ltd.. All Rights Reserved

Fill The Form